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Active Not RecruitingPhase 1NCT04211714

Study to Evaluate of EXG34217 in Patients With Telomere Biology Disorders With Bone Marrow Failure

This is a Phase I/II, open label, single center study to assess the safety and tolerability of EXG34217 in bone marrow failure patients with telomere biology disorders.

Lead sponsor: Elixirgen Therapeutics, Inc.•1 U.S. locations•View source on ClinicalTrials.gov

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Data from ClinicalTrials.govLast updated on ClinicalTrials.gov: February 6, 2026Terms

Trial snapshot

StatusACTIVE_NOT_RECRUITING

PhasePHASE1

Enrollment12

Start dateApr 2021

Last updatedFeb 6, 2026

Condition

Telomere Shortening Bone Marrow Failure

Locations shown

Cincinnati Children's Hospital

Cincinnati, Ohio

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Data Source & Attribution

This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.

ClinicalTrials.gov last update: February 6, 2026Data synced to Clareo: May 25, 2026

Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.

Neither the United States Government nor Clareo Health make any warranties regarding the data. Check ClinicalTrials.gov frequently for updates.

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