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Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells | Clinical Trials | Clareo Health

COMPLETEDPhase 1NCT00001234

Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells

Gaucher's disease is a lysosomal storage disease resulting from glycocerebroside GLUCOCEREBROSIDE (1) accumulation in macrophages due to a genetic deficiency of the enzyme glucocerebrosidase. It may o...

Lead sponsor: National Institute of Neurological Disorders and Stroke (NINDS)•1 U.S. locations•View source on ClinicalTrials.gov

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Data from ClinicalTrials.govLast updated on ClinicalTrials.gov: March 4, 2008Terms

Trial snapshot

StatusCOMPLETED

PhasePHASE1

Enrollment120

Start dateJan 1988

Last updatedMar 4, 2008

Condition

Gaucher's Disease

Locations shown

National Institute of Neurological Disorders and Stroke (NINDS)

Bethesda, Maryland

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Data Source & Attribution

This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.

ClinicalTrials.gov last update: March 4, 2008Data synced to Clareo: June 28, 2026

Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.

Neither the United States Government nor Clareo Health make any warranties regarding the data. Check ClinicalTrials.gov frequently for updates.

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